Product approvals in regenerative medicine and rare diseases are among the highlights in our recap of recent FDA regulatory decisions.

The majority of patients have at least one F508del mutation. TRIKAFTA’s mechanism aims to correct the defective CFTR protein, improving salt and water flow in cells and alleviating symptoms. The FDA ...

The majority of patients have at least one F508del mutation. TRIKAFTA's mechanism aims to correct the defective CFTR protein, improving salt and water flow in cells and alleviating symptoms. The FDA ...

Vertex Pharmaceuticals (VRTX) announced the U.S. Food and Drug Administration has approved the expanded use of Trikafta for the treatment of people with cystic fibrosis ages 2 and older who have ...

The majority of patients have at least one F508del mutation. TRIKAFTA's mechanism aims to correct the defective CFTR protein, improving salt and water flow in cells and alleviating symptoms.

BOSTON--(BUSINESS WIRE)--Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced the U.S. Food and Drug Administration (FDA) has approved the expanded use of TRIKAFTA ® (elexacaftor ...

Share on Facebook. Opens in a new tab or window Share on X. Opens in a new tab or window Share on LinkedIn. Opens in a new tab or window The FDA approved a once-daily oral combination of ...

Trikafta, a drug approved for use in Canada in 2021 that dramatically improves the functioning of the lungs, has revolutionized treatment and significantly increased the life expectancy of people ...

It operates via a molecular "cut and paste" mechanism driven by special proteins, known as recombinases. The integron system has been researched a lot. Some bacteria gain new resistance very fast ...

The company’s product portfolio includes Trikafta, Symdeko/Symkevi ... of-the-art technology platforms to discover new disease targets, compounds, delivery mechanisms, and treatment modalities. Vertex ...

KYIV, Dec 15 (Reuters) - Ukrainian President Volodymyr Zelenskiy said on Saturday he had instructed his government to set up supply mechanisms to deliver together with international organisations ...