CRISPR Therapeutics, whose CEO is Samarth Kulkarni, and Vertex Pharmaceuticals earned the first U.S. Food and Drug ...

In the UK, approximately 17,500 people have sickle cell disease and 300 babies are born with the condition each year. It is a genetic disorder caused by inherited mutations in a person's DNA that ...

David Liu couldn’t sleep after the U.S. Food and Drug Administration cleared the first clinical trial based on his research.

Martin Mwita, 20, is the first patient in St. Louis and among the first across the country to receive a new gene therapy for sickle cell disease.

In December 2020, the New England Journal of Medicine published a paper titled CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia, marking an exciting new chapter in the treatment of ...

The quality of life of patients with sickle cell anemia is severely compromised similar to or even worse than patients with other chronic diseases such as arthritis. Patients who responded to ...

Hydroxyurea remains effective long-term in reducing emergency department visits and hospital days for children living with sickle cell disease ... improving anemia, and reducing the risk of ...

Bhopal: Governor Mangubhai Patel inaugurated the genetic analysis laboratory and DNA sequencer machine at BMHRC's sickle cell anaemia competence centre. He also launched a seminar titled "Genetic ...

Kennedy Jr. said 35 states have agreed to participate in a federal pilot program aimed at helping Medicaid patients access costly gene therapies for sickle cell disease. The states represent about ...